Resources:

Community, Leukodystrophy Centers & Genetic Reports

TUBB4A-related leukodystrophy patients often require a range of therapies and visits to specialists to address symptoms. The extensive care demands can leave caregivers feeling drained, overwhelmed, and socially isolated. The impact of TUBB4A mutations extends beyond symptom management, affecting various aspects of family life. It's essential to build a support network, including family, friends, therapists, and respite care. Don't hesitate to seek help and share your feelings. Connect with other parents and legal guardians facing similar challenges by joining the private TUBB4A Parent Facebook group for support and understanding.

Understanding your Genetics Report

Understanding a genetic test report can feel overwhelming at first, with all the technical terms and symbols. If you're puzzled by your report, a genetic counselor is the best person to help decode it. Still, we know you might have more questions afterward, so we've put together this guide to offer further assistance.

Leukodystrophy Centers

These are some notable centers around the world that specialize in the diagnosis, treatment, and research of leukodystrophies:

Kennedy Krieger Institute, Johns Hopkins Medicine

Baltimore, Maryland

Children's Hospital of Philadelphia (CHOP)

Philadelphia, Pennsylvania

National Institutes of Health (NIH)

Bethesda, Maryland

Mayo Clinic

Rochester, Minnesota

Children's Hospital Boston

Boston, Massachusetts

UCSF Benioff Children's Hospital

San Francisco, California

Great Ormond Street Hospital

London, England

Hospital Sant Joan de Déu Barcelona

Barcelona, Spain

San Raffaele Scientific Institute

Milan, Italy

Please note that availability of services and expertise may vary among these centers, and it's advisable to contact them directly for specific information regarding leukodystrophy care and research. Additionally, new centers may emerge over time, so it's worth keeping an eye on the latest developments in the field.

Organizations you might find helpful:

n-Lorem Foundation

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IPSEN Cares

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HopeKids

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n-Lorem Foundation ~ IPSEN Cares ~ HopeKids ~

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